First Oral Treatment For Spinal Muscular Atrophy Gets EMA Nod

Two Of Six Drugs Recommended For EU-Wide Use Have Orphan Designation

 
• By Vibha Sharma
  
Surgical doctor looking at radiological spinal x-ray film for medical diagnosis on patient’s health on spine disease, bone cancer illness, spinal muscular atrophy, medical healthcare concept
Current treatments for SMA involve frequent clinic visits or invasive procedures • Source: Shutterstock
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