Commercial opportunity for Mepsevii is small, but launch paves way for company's second product burosumab, following on its heels.
Ultragenyx Pharmaceutical Inc.is planning to launch its first drug Mepsevii for the rare genetic disease Mucopolysaccharidosis VII, also called Sly syndrome, in the US with a lean commercial effort, while simultaneously planning for the introduction of its second product burosumab, which is currently under review.
The US FDA approved Mepsevii (vestronidase alfa-vjbk), a recombinant version of the enzyme beta-glucuronidase, for the treatment of children and...
The world’s biggest pharmaceutical companies mostly saw growth in 2024 but 2025 promises to be more of a mixed bag with headwinds including losses of exclusivity, Medicare Part D redesign and challenges in the Chinese market.
The nod will help unlock a national market for the partners’ Dupert (fulzerasib) in which roughly 50,000 people are expected to be newly diagnosed with lung cancer harboring the KRAS G12C mutation in 2025. Meanwhile, two other homegrown rivals are also closing in on marketing clearances in China.
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Mounjaro, Eliquis, and Darzalex buck the Q1 trend to make gains
