A Runaway Hit In US, Pfizer Gains EU Nod for Vyndaqel In Cardiomyopathy

Company Considers Using AI To Boost Diagnoses

Vydaqel saw its uptake take off in the US last year. UK’s NICE to pass judgement on cost effectiveness by June.

NEW YORK CITY - MAY 2015: Metal plate logo of Pfizer in his headquarters building. Pfizer is an American multinational pharmaceutical corporation, one of the world's largest pharmaceutical companies.

Pfizer’s rare disease treatment Vyndaqel (tafadamis) proved to be one of most notable outperformers in new US drug launches in 2019, and the company has now gained approval for the same use in Europe.

Vyndaqel gained US FDA approval in May last year as a treatment for cardiomyopathy in adult patients with the rare...

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