Alexion/AstraZeneca has announced positive top-line results from the Phase III study of ALXN1840 in patients with the rare genetic disorder, Wilson disease, including in patients already on standard-of-care therapies. The compound is ahead of two candidate gene therapies from other companies at early-stage clinical development.
AstraZeneca PLC’s rare disease unit Alexion has announced positive results with ALXN1840 in the Phase III FoCus study in Wilson disease, and the compound is expected to be submitted for marketing approval in coming months.
The promising news follows the disappointment of a week ago, when the Alexion unit reported poor results with another late-stage...
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