Vertex Expands In Vivo Gene-Editing Plans With Verve Liver Disease Pact

Complements Presence In Ex Vivo And Cell Therapy

Vertex is expanding its investments across advanced therapies again, R&D chief David Altshuler adding a second in vivo gene-editing deal to its pipeline.

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Vertex is investing in cell therapy and ex vivo and in vivo gene editing platforms. • Source: Shutterstock

Vertex has signed a major deal with Verve Therapeutics to develop an in vivo gene editing therapy for an unnamed liver disease, underlining its determination to be a major player in the burgeoning field.

Boston, MA-based Vertex is currently reaping the benefits of its hugely successful small molecule cystic fibrosis drugs, which will swell...

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