Sales Of BioMarin’s Hemophilia Gene Therapy Move At Glacial Pace

Three Patients Treated In 2023

 
• By Alaric DeArment
  
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Analysts had forecast Q4 Roctavian sales of $5m-$6m, but they came in shy of $3m, and uptake has not yet come to reflect apparent demand.

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While BioMarin Pharmaceutical Inc.’s total fourth quarter and full year 2023 revenues rose from the comparable period in 2022, the launch of its hemophilia A gene therapy Roctavian (valoctocogene roxaparvovec-rvox) has been significantly slower than analysts had hoped, and the company suggested that uptake has not yet caught up with signs of market demand.

The biotech company reported fourth quarter revenues on 22 February of $646.2m, a 20% year-over-year increase, while full-year 2023 revenues...

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