Momentum Builds For Tomorrow's More Convenient Hemophilia Drugs

 
• By Emily Hayes
  
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Updates for a range of new therapies from Roche, Alnylam, BioMarin and Spark Therapeutics at the ISTH meeting in Berlin show progress in development of new hemophilia alternatives, with more late-stage programs kicking off.

3-D Rendering Red Blood Cells

The International Society on Thrombosis and Haemostasis (ISTH) Congress in Berlin provided a showcase for a new wave of hemophilia therapies to shine and advance – Roche'sbispecific antibodyemicizumab and Alnylam Pharmaceuticals Inc./Sanofi's RNA-interference therapy fitusiran as well as gene therapies from BioMarin Pharmaceutical Inc. and Spark Therapeutics Inc.

The ISTH meeting, held July 8-13, featured data for innovative therapies aspiring to compete with today's standard of care, including...

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